A single injection into the bloodstream of a mouse corrected a mutation linked to autism in neurons throughout the brain and ...

Multiple new studies are advancing understanding of autism spectrum disorder by linking specific genes, brain structures, and prenatal factors to its development. Research spans from identifying rare ...

Company advances its leadership in MASH with clinical-stage, genetically targeted siRNA asset from Arrowhead PharmaceuticalsPrecision approach ...

Arrowhead Pharmaceuticals, Inc. today announced an exclusive worldwide license agreement with Madrigal Pharmaceuticals for ARO-PNPLA3, Arrowhead's clinical stage RNA interference (RNAi) therapeutic ...

Gene syntax alters DNA supercoiling to amplify or suppress nearby genes. This could improve the effectiveness of gene ...

A global pharmaceutical company already investing over $20 billion to operations in the United States is tossing in millions ...

Design Therapeutics Inc (DSGN) reports encouraging advancements in their RESTORE-FA trial, with key data expected later this year, despite early-stage challenges.

Jonathon Baker, Ph.D., uses advanced sequencing to develop treatments for oral infections Jonathon Baker, Ph.D., assistant ...

The developer says its project will help the River City’s housing undersupply—and a leading builder says he’s keen for the ...

Right now, TerraBlaster's tech works at 5mph, a speed CEO Jorge Heraud reckons he can double to 10mph “pretty soon.” ...

Calorie restriction lowers C3, an immune protein tied to aging and inflammation, improving health without requiring weight ...

Novartis is hardly alone in staking out manufacturing space in the Triangle. The Morrisville project lands as other big ...