A single injection into the bloodstream of a mouse corrected a mutation linked to autism in neurons throughout the brain and ...

Ascidian Therapeutics, a biotechnology company seeking to treat human diseases by rewriting RNA, announced the completion of the adult dose escalation portion of the STELLAR phase 1/2 clinical trial ...

A stabilized mRNA carrier turns tumor injection into broader immune activation by extending vaccine delivery to lymph nodes ...

Ascidian Completes Dose Escalation Portion Of Phase 1/2 STELLAR Trial Of ACDN-01 For Stargardt Disease And Announces Expanded Clinical Study Plans. STELLAR to begin enrolling pediatric subjects STARPA ...

Combriax demonstrates strong immunogenicity across age groups, exceeding comparator vaccines for multiple influenza strains ...

Rabies is a vaccine-preventable, zoonotic, viral disease which affects the central nervous system. Rabies vaccine is given ...

Scientists have developed a breakthrough injectable biomaterial that travels through the bloodstream to repair damaged tissue ...

Quarterly RNA drug plozasiran turns off a liver gene, sharply lowering life‑threatening pancreatitis attacks in a rare genetic disorder.

A new breakthrough could change how high cholesterol is treated, offering a powerful alternative to traditional drugs. Researchers have developed tiny DNA-based molecules that shut down PCSK9—a key ...

The EMA has recommended updating Comirnaty 10 mg formulations, including JN.1, KP.2, and LP.8.1 versions, to allow COVID-19 vaccination in individuals aged 6 months or older.

ATTR-CM is a heterogeneous and rapidly progressive disease, and patients often present with complex clinical profiles. At Heart Failure 2026, Alnylam will present multiple new analyses from the Phase ...